Latest Genetic Disorders news
Lentiviral Gene Therapy Shows Sustained Clinical Efficacy for ADA-SCID
posted October 17th
by modernClinician Editorial Team
by modernClinician Editorial Team
FDA Grants Accelerated Approval for First Treatment for Barth Syndrome
posted September 25th
by modernClinician Editorial Team
by modernClinician Editorial Team
Apitegromab Improves Motor Function in Spinal Muscular Atrophy
posted August 25th
by modernClinician Editorial Team
by modernClinician Editorial Team
Long-Term Gantenerumab May Slow Decline in Dominantly Inherited Alzheimer Disease
posted March 25th
by modernClinician Editorial Team
by modernClinician Editorial Team
Most Specialty Oral Anticancer Meds for Blood Cancers Are Initially Rejected by Insurers
Drug Interactions Reducing Contraceptive Effectiveness Common in Epilepsy
Holding DMARDs at Time of COVID-19 Vaccine Not Warranted in Those With Inflammatory Arthritis
1 in 3 With Lupus Take Supplements, Medications With Potential for Interactions
Congenital Ichthyosis Linked to Allergic Disorders
Oral Engasertib Safe for Hereditary Hemorrhagic Telangiectasia
Adenotonsillectomy Safe in Children With Down Syndrome, Other Genetic Syndromes
Lamotrigine, Mexiletine Show Similar Benefits for Nondystrophic Myotonias