Latest Genetic Disorders news
FDA Grants Accelerated Approval for First Treatment for Barth Syndrome
posted September 25th
by modernClinician Editorial Team
by modernClinician Editorial Team
Apitegromab Improves Motor Function in Spinal Muscular Atrophy
posted August 25th
by modernClinician Editorial Team
by modernClinician Editorial Team
Long-Term Gantenerumab May Slow Decline in Dominantly Inherited Alzheimer Disease
posted March 25th
by modernClinician Editorial Team
by modernClinician Editorial Team
FDA Approves Kebilidi for Aromatic L-Amino Acid Decarboxylase Deficiency
posted November 27th
by modernClinician Editorial Team
by modernClinician Editorial Team
Cretostimogene Promising for High-Risk, Non-Muscle-Invasive Bladder Cancer
Aglatimagene Besadenovec + Valacyclovir Ups DFS in Localized Prostate Cancer
Most Speakers at FDA Advisory Committee Meetings Support Drug Approval
Oral Engasertib Safe for Hereditary Hemorrhagic Telangiectasia
Adenotonsillectomy Safe in Children With Down Syndrome, Other Genetic Syndromes
Lentiviral Gene Therapy Shows Sustained Clinical Efficacy for ADA-SCID
Lamotrigine, Mexiletine Show Similar Benefits for Nondystrophic Myotonias
Risk for Venous Thromboembolism Up for Those With Sickle Cell Trait